Volume 90%
Press shift question mark to access a list of keyboard shortcuts
Keyboard Shortcuts
Play/PauseSPACE
Increase Volume
Decrease Volume
Seek Forward
Seek Backward
Captions On/Offc
Fullscreen/Exit Fullscreenf
Mute/Unmutem
Seek %0-9
00:00
00:00
00:00
 

Chapters

Transcript

Video

Q&A About the Use of Gene Transfer Therapy for the Treatment of Rare Pediatric Neurologic Disorders

Pediatric neurologist Tom Crawford discusses how gene transfer therapy is being used to treat rare neurologic diseases in children, how it’s used at Johns Hopkins to treat infants diagnosed with spinal muscular atrophy (SMA), and challenges the field of gene transfer therapy must address in the near future.

Related Presenters

Thomas Crawford, MD.

Thomas Crawford, MD

Dr. Tom Crawford has been a member of the Department of Neurology since 1987. He is co-director of the MDA clinic for Neuromuscular Disorders and Neurologist for the Ataxia Telangiectasia Clinical Center at Johns Hopkins. His practice ...

View full profile

ADVERTISEMENT

Related Videos